ASMD and Niemann-Pick Disease Research Programs

Conducts targeted research on Acid Sphingomyelinase Deficiency and Niemann-Pick disease, including gene therapy, FAAH inhibition, biomarker discovery, and real-world evidence studies.

what makes this distinct Focuses specifically on preclinical and translational research for rare lysosomal storage disorders—ASMD and Niemann-Pick types A and A/B—using model organisms, genetic therapies, and patient data, rather than broad clinical trials or general neurological research.

organizations

1 orgs in this cluster's subtree

Every organization with primary activities in ASMD and Niemann-Pick Disease Research Programs or any of its descendants. Click a column header to sort. Filter by name or state above the table.

showing 1 of 1

#	Organization	State	Revenue	Activities ↓
1	WYLDER NATION FOUNDATION Wylder Nation Foundation is a nonprofit organization focused on improving the lives of children affected by Lysosomal Storage Diseases, particularly Acid Sphin…	AZ	$551K	6