4 ORGS · 10 ACTIVITIES · 2 STATES ← back to explorer ·
program type

Sickle Cell Disease Gene Therapy Access

Advocates for and supports patient access to gene therapies and related treatments for sickle cell disease, including policy engagement and public awareness.

what makes this distinct Focuses specifically on expanding access to emerging gene therapies like Casgevy and Lyfgenia for sickle cell disease, rather than conducting clinical trials or broader medical research.

4
organizations
10
activities
0
child clusters
0
strategies
coverage AZ 3 · CA 1
NTEE codes
G43E86E70Z
organizations

4 orgs in this cluster's subtree

Every organization with primary activities in Sickle Cell Disease Gene Therapy Access or any of its descendants. Click a column header to sort. Filter by name or state above the table.

showing 4 of 4
#OrganizationStateRevenueActivities
1ARIZONA BLOOD ALLIANCE INC
Arizona Blood Alliance (ABA) is a nonprofit organization dedicated to improving the lives of Arizonans with inherited blood disorders, including hemophilia, vo…
AZ$110K4
2LUCAS JOHN FOUNDATION INC
LUCAS JOHN FOUNDATION INC is a nonprofit organization founded by the parents of Lucas Culp, a child diagnosed with the rare genetic disorder Nonketotic Hypergl…
AZ$224K3
3Public Health Institute
Public Health Institute advances evidence-based strategies to prevent chronic and communicable diseases, promote health equity, and strengthen public health sy…
CA$243.6M2
4DEL CORAZON DE JESUCRISTO
Del Corazón de Jesucristo is a faith-based medical ministry operating in El Catey, Dominican Republic, founded by Dr. Steve Dorsey after a 1986 mission trip. T…
AZ$50K1