5 ORGS · 15 ACTIVITIES · 1 STATES ← back to explorer ·
program type

Gene Therapy Access Advocacy

Advocates for patient access to gene therapies and investigational treatments for rare and genetic diseases, particularly sickle cell disease and ultra-rare conditions.

what makes this distinct Focuses on policy advocacy and patient access to emerging gene-based treatments, rather than conducting research or providing direct clinical care.

5
organizations
15
activities
0
child clusters
5
strategies
coverage AZ 5
NTEE codes
G43H99E86
organizations

5 orgs in this cluster's subtree

Every organization with primary activities in Gene Therapy Access Advocacy or any of its descendants. Click a column header to sort. Filter by name or state above the table.

showing 5 of 5
#OrganizationStateRevenueActivities
1ARIZONA BLOOD ALLIANCE INC
Arizona Blood Alliance (ABA) is a nonprofit organization dedicated to improving the lives of Arizonans with inherited blood disorders, including hemophilia, vo…
AZ$110K5
2CRITICAL PATH INSTITUTE
Critical Path Institute (C-Path) is a nonprofit organization focused on improving and streamlining drug development processes through collaboration among indus…
AZ$31.2M4
3LUCAS JOHN FOUNDATION INC
LUCAS JOHN FOUNDATION INC is a nonprofit organization founded by the parents of Lucas Culp, a child diagnosed with the rare genetic disorder Nonketotic Hypergl…
AZ$224K3
4BARRY GOLDWATER INSTITUTE FOR
The Goldwater Institute is a conservative and libertarian public policy think tank that advocates for limited government, individual liberty, and free markets.…
AZ$7.8M2
5DEL CORAZON DE JESUCRISTO
Del Corazón de Jesucristo is a faith-based medical ministry operating in El Catey, Dominican Republic, founded by Dr. Steve Dorsey after a 1986 mission trip. T…
AZ$50K1
theories of action

strategies used in this cluster

Theories of action extracted from orgs in this subtree. Click any to see the full set of orgs running the same approach.